Fetal molecular therapies show promise in studies of MPS7 mice

In mouse study, stem cells migrated to proper locations in fetal brain and body, differentiated into cells that produce crucial missing protein.

Administering stem cell or enzyme therapy in utero may be a path to alleviating some congenital diseases that often result in losing a pregnancy, according to a new study in mice by UC San Francisco researchers, who showed that stem cells can enter the fetal brain during prenatal development and make up for cells that fail to make an essential protein.

UCSF News: In Utero Stem Cell Transplants, Enzyme Replacement May Offer New Treatments for Deadly Metabolic Disorders